Nonclinical findings provide evidence of the mechanism of action of nomlabofusp and support the potential use of skin FXN concentrations as a novel surrogate endpoint for Larimar’s planned BLA ...

Critics will argue that double-blind placebo-controlled trials provide more reliable information than real-world clinical ...

A recent review confirms the safety and efficacy of biosimilar insulins, addressing concerns and promoting their adoption for ...

Pro-life medical groups are urging Health and Human Services Secretary Robert Kennedy Jr. to reexamine the FDA’s broad ...

Rare genetic diseases are challenging for patients and their families—made all the more overwhelming because symptoms tend to ...

Ophthalmology Times connects eye care professionals with surgery, imaging, gene therapy, & diagnostic advances to enhance ...

Syndax now has two approved therapies, but the share price remains under pressure despite these milestones. See why SNDX ...

Here are the key takeaways from the full Times Magazine story about the F.D.A.: The F.D.A.’s regulators have an enormous ...

Jeneen Interlandi, a domestic correspondent for Opinion and a staff writer at the magazine, writes frequently about public health. For this article, she interviewed dozens of people who have worked ...

Novartis ( NYSE: NVS) on Tuesday said that Coartem (artemether-lumefantrine) Baby has been approved by Swissmedic as the ...

"No More Tears," by Gardiner Harris, is a scathing expose of Johnson & Johnson and its many missteps and transgressions.