Four decades have passed since cochlear implants gave infants born deaf the ability to hear. Now, gene therapy promises to ...

Biotechs in the charter city of Próspera aim to cure aging, but experts question the feasibility of their goals.

Mixed headlines have plagued the cell and gene therapy space of late. We believe that a renewed case of optimism is not only ...

The search for gene therapies to treat rheumatoid arthritis (RA) has moved in fits and starts over the past two decades, with trials starting and stopping, and their focus shifting to osteoarthritis ...

Tiny immune cells called microglia protect the central nervous system (CNS) in a multitude of ways: They provide innate ...

Progress of in vivo gene therapy for use in malignancies, monogenic disorders, and degeneration disease. AAV, adeno-associated virus; TK, thymidine kinase; ADA-SCID, adenosine deaminase-deficient ...

Gene therapy has undergone a renaissance in recent years, with several drugs offering beneficial, even life-saving treatments, now approved by the FDA. One example was reported earlier this year, with ...

Boston biotech Beam Therapeutics has announced initial data from a phase 1/2 trial of its gene therapy for a genetic lung and liver disease, with no serious adverse events reported among the nine ...

The cell and gene therapy CRO market presents growth opportunities driven by FDA-approved therapies, over 90 global approvals, and 3,500 trials across 16 therapeutic areas, primarily in North America.