Cystic fibrosis (CF) is a rare autosomal recessive disorder that affects numerous systems of the body. It is a complicated disease that differs from person to person. An autosomal recessive disorder ...

Cystic fibrosis is caused by genetic changes and is always present at birth. Although rare, cystic fibrosis isn’t diagnosed in some people who have mild symptoms until they’re adults. This is known as ...

Cystic fibrosis (CF) is a disease that people can be born with. While there is no cure, people with CF may live well into adulthood if they receive the appropriate treatment and medical monitoring.

Cystic fibrosis, a genetic disorder, affects lungs and other organs. It causes thick mucus buildup. Researchers have identified over 2,000 gene mutations. New treatments called CFTR modulators are now ...

Antisense oligonucleotides, or ASOs, are molecules that can be used to control protein levels in cells. Scientists have discovered a new way ASOs may help cells produce a protein missing in cystic ...

Patients with cystic fibrosis (CF) and elevated blood eosinophil counts had significantly increased respiratory symptoms compared to those with lower eosinophil counts, based on data from 109 ...

As an undergraduate student in the early 1980s, Marie Egan volunteered at the Children’s Hospital of Philadelphia. She’d often spend time in the hospital playrooms with children with serious illnesses ...

The desire to have children represents one of the most fundamental human experiences, yet for people living with cystic fibrosis, the path to parenthood can feel uncertain and complex. You might ...

A young girl with cystic fibrosis whose lungs were functioning at just 67 percent is running around again thanks to a miracle drug recently added to the NHS funding list. Harriet Corr, seven, is ...

Antisense oligonucleotides, or ASOs, are molecules that can be used to control protein levels in cells. Cold Spring Harbor Laboratory Professor Adrian Krainer leveraged ASO technology to develop the ...